Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s ...

Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...

The funding will accelerate the development of Fuse's technology platform and pipeline of novel gene therapies. With its ...

Qure's stock rises on Huntington's therapy progress and strong gene therapy pipeline. Learn about QURE stock's cost-cutting ...

When a test determined that Walter had hemophilia, his Omaha owner joined a group seeking to raise $50,000 for a clinical ...

Trial at the Johns Hopkins Kimmel Cancer Center and other centers finds reduced-intensity haploidentical bone marrow ...

YolTech's gene therapy is intended as a one-time life-long cure for patients living with PH1, which can lead to kidney ...

In Regeneron Pharmaceuticals Inc.’s phase I/II Chord study of 12 children with genetic hearing loss, 10 out of 11 have shown improvements after being treated with a gene therapy. “What is really ...

Partnership aims to utilize real-world insights on more than 70,000 de-identified patients with retinitis pigmentosa to advance gene therapy treatmentsSAN FRANCISCO, Feb. 25, 2025 (GLOBE NEWSWIRE) -- ...

Ligand originated, structured, and invested $50 million and led a syndicate of co-investors who invested $25 million in ...

Precigen on Tuesday said a green light would make PRGN-2012 the only FDA-approved therapeutic for the treatment of adults with the disorder, which is a lifelong neoplastic disease of the upper and ...