CompareNetworks is proud to announce the publication of the first issue of Cell & Gene Therapy Review, marking a significant ...
Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...
When a test determined that Walter had hemophilia, his Omaha owner joined a group seeking to raise $50,000 for a clinical ...
High dose and low dose of TSHA-102 continue to be generally well tolerated with no treatment-related SAEs or DLTs in all ...
High dose and low dose of TSHA-102 continue to be generally well tolerated with no treatment-related SAEs or DLTs in all pediatric, adolescent and adult patients treated (high dose, n=6; low dose, n=4 ...
"Jim brings a specialized skillset and innovative technology experience at the start of what will be a year of momentum for ...
Qure's stock rises on Huntington's therapy progress and strong gene therapy pipeline. Learn about QURE stock's cost-cutting ...
YolTech Therapeutics reports positive clinical data for YOLT-203, an in vivo gene editing therapy for primary hyperoxaluria type 1: Shanghai, China Wednesday, February 26, 2025, 1 ...
Trial at the Johns Hopkins Kimmel Cancer Center and other centers finds reduced-intensity haploidentical bone marrow ...
Vriddhi, a seven-month-old girl, is battling spinal muscular atrophy type 1, a rare progressive disease that will cause her muscles to weaken over time. The only hope for her survival is a gene ...
Pharmaceutical Technology on MSN20 時間
FDA removes clinical hold on Entrada’s Duchenne therapy
Entrada Therapeutics can plough on with the development of its Duchenne muscular dystrophy (DMD) therapy, ENTR-601-44, now ...
New research reveals that voluntary exercise restores STAT3 levels in the amygdala, helping to prevent stress-induced ...